Rare Disease Drug Gets Tailored FDA Guidance Before Pivotal TrialsBusiness PenMay 5, 2026May 25, 2026 May 5, 2026May 25, 2026 [stock_market_widget type=”card” template=”basic2″ assets=”IRD” realtime=”true” api=”yahoo-finance”] An early-stage gene-therapy program targeting a rare form of childhood blindness has quietly entered a new lane inside the...